Kunming First People's Hospital, Pediatric Ward.

Since all intravenous drugs, such as subcutaneous injection drugs, intramuscular injection drugs, etc., require clinical trials in the hospital, the hospitalization time is usually 1-3 days.

Of course, the treatment interval is also the non-medication time, and the patient can rest at home.

Therefore, after Cao Yang received the news of the successful development of genetic medicine, he immediately rushed to the designated cooperative hospital of Sanqing Pharmaceutical with his son Xiaowei to officially launch clinical trials.

Seeing a needle pricking into his son Xiaowei's vein, Cao Yang's face became nervous.

After all, it was the first time to use genetic drugs. Although the animal experiments were very successful, he still felt a little uneasy.

According to the plan, zfn will be delivered into the body, and each injection can cover a certain range of somatic cells. Somatic cells will undergo genome editing, and the diseased genes will be repaired.

However, since the menkes disease gene is expressed in many places in the body, it is unlikely that a single injection can cover all somatic cells in the body.

Theoretically, patients also need regular injections every few months.

Although the duration is relatively long, patients do not need to be hospitalized every time. They only need to get an injection in the outpatient clinic. For most patients, this will not cause any burden.

When all adult stem cells in the body have undergone gene editing and are cured, then the new cells they produce will be healthy cells, and the patient will be completely cured.

Half an hour later, the injection was completed, and Cao Yang felt relieved when he saw that his son had no abnormal symptoms.

Children need to stay in the ward for a few days to observe the specific curative effect.

On the third day, the doctor looked at the physical examination report and nodded with satisfaction: "The child's physical examination was normal, and the laboratory test of serum copper and ceruloplasmin has also returned to normal levels. Next, you remember to take regular injections every three months.

To see the effects."

Cao Yang clenched his fists, feeling extremely excited. Looking at his son who was sleeping soundly, he couldn't help but burst into tears.

All the dedication and hard work finally paid off.

My son was finally saved.

Typical patients with this disease usually die within 3 years of age, and only a few with mild symptoms can survive until the age of 20. This cannot change the fate of eventual death.

Over the past two years, he had been desperately chasing and racing against death, and finally he was able to get ahead of death and save his son from the brink of life and death.

I no longer have to worry about my son not surviving until he is 3 years old.

After the doctor left, he quickly shared the good news in the group.

The group of patients suddenly burst into cheers.

"That's great, our children have been saved."

"Xiaowei looks pretty good, he seems to be really well."

"Thank you, Brother Cao. All this is thanks to you. If you hadn't been running around and doing so much, the children wouldn't be where they are today."

"Thank you Brother Cao."

"I would also like to thank Sanqing. If they hadn't been willing to lend a helping hand, we don't know when we would have seen the advent of genetic medicine."

"Fortunately, there is such a high-tech pharmaceutical company in China that can develop high-tech products such as genetic medicines. This is all because of the strength of the country, which has led to the rise of all walks of life."

"Yeah, I still remember that we used to use imported medicines when we were sick. Domestic medicines were not very effective. Now I go to the hospital to see a doctor. For some daily medicines, the doctor recommends Sanqing to me. They say they are more effective than imported medicines. And then it’s cheaper.”

"The rise of domestically produced drugs has led to the emergence of today's genetic drugs. I am really more patriotic now than ever before and feel proud that I was born in China."

"Haha, that must be the case. There is no cure for this disease abroad. Genetic medicines are only available in China. Even foreigners would envy us."

"When will the clinical trials officially begin? We can't wait."

"Hey, wait a minute, I received a notification from Longtu. It seems that the clinical trial has officially started. Go and sign up."

"So fast, I'll go right away."

The patients clicked into the app at the speed of light, and sure enough, the ‘clinical trial application’ function was already available.

Grain dust

They filled in some relevant information, signed and uploaded it, and submitted the application quickly.

There were not many people, only 60 people, so they all passed quickly.

Because the disease menkes is so rare and there are only so many people in China, when Sanqing applied for clinical trials, it directly put the first and second clinical phases together. As for the third clinical phase, it may have to go abroad to find some patients. Participated.

It is estimated that by the time it is launched, there will only be a few hundred patients left in the world. With such a small market, no wonder no other pharmaceutical companies are willing to do it.

That is to say, Sanqing wants to combine all rare diseases and conduct unified research as single-gene genetic diseases, and then they are willing to invest in such an unpopular disease.

Otherwise, it is estimated that Cao Yang would be the only one fighting alone and relying on his own efforts.

Even if he finally achieves results, it may be several years later.

Whether Xiaowei will still be alive by then is a matter of debate.

Therefore, no one understands the difficulties of genetic medicine better than the families of these children, and no one is more grateful to Sanqing than them.

Even with cancer, some patients can still survive treatment, but with Alzheimer's disease, the patients are all elderly and the chance of death is not high.

The only patients with rare diseases are infants, and most of them have no cure. They often die early before the age of five, leaving huge trauma and grief in their parents' lives.

From this point of view, Sanqing Pharmaceutical’s actions are the reborn parents of patients with rare diseases.

No matter how grateful the family members are, they cannot be exaggerated.

They almost wanted to build an immortal memorial arch for Wei Kang, and knelt down day and night.

Sanqing soon held a press conference to announce the launch of the first gene therapy drug in China.

As soon as the news was released, the media were shocked and immediately wrote news reports with great excitement and published them all over the Internet.

This is big news!

Gene therapy! Isn’t this something only in science fiction? It has become a reality.

No matter how serious the media was, they were all shocked at this moment. Every statement they made was astonishing, and they wanted to shock the attention of netizens across the country. They could exaggerate as much as they wanted.

"Shocking! Sanqing successfully developed gene therapy drugs to overcome the rare disease menkes!"

"Shocked! China will enter the era of gene editing!"

"Shocking! Science fiction becomes reality. How long will it take for us to move from gene therapy to genetic evolution?"

"A brief talk about future medical treatment in the era of gene editing!"

"Top ten technologies that have changed mankind, the past and present of gene editing technology!"

The media also dug up old news about Cao Yang from a year ago, conducted an in-depth interview with him and other menkes family members, and made a special program on gene-editing drugs.

Netizens were so shocked by Sanqing's SMA gene medicine before that they couldn't recover from it. Now two months have passed and they are shocked again.

Seeing the research results of Sanqing popping up one after another, netizens were so excited that they became a little numb.

"Sanqing is awesome! Mr. Wei is so awesome."

"Although menkes is a disease that has few patients, it is extremely painful for patients and their families. Thanks to You Sanqing, who is willing to expend energy to conquer this disease, dozens of patients have been saved again."

"What a miracle and how great this is. I'm so touched."

"Cao Yang, who made homemade medicine for his son, is also touching. In this world, he is not afraid of troubles, but of people with good intentions. Such a father is truly a role model for our generation."

"How come the genetic drug Sanqing was developed so quickly? It's like a hen laying eggs. I'm so numb that I can't say anything except applaud."

"1. There is no fluctuation in my heart, I just feel that it is natural."
Chapter completed!